| Publication Type: | Article |
| Journal Name: | JAMA |
| Full Citation: | Kesselheim, Aaron, JAMA. 2016;316(22):2357 doi:10.1001/jama.2016.16437 |
| External Link: | Approving a Problematic Muscular Dystrophy Drug: Implications for FDA Policy |
| Media Source: | JAMA |
| People: | Aaron Kesselheim |